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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Inbred C57BL
Génomique
Dystrophin-EGFP
Myotendinous junction
L-Type
LncRNA
Cardiomyopathie
Homeostasis
Autophagy
Diseases
Becker BMD muscular dystrophy
Male
Antisense oligonucleotides
DHPR α1S
Cachexia
Mice
CaV subunits
Molecular Sequence Data
Dystrophy
Becker muscular dystrophy
Knockout
Duchenne DMD dystrophy
Energy Metabolism/drug effects
Cardiomyopathy
Becker muscular dystrophy BMD
BMD
Dystrophin
Modificateurs de gènes
Muscle Strength
Muscle development
Dystrophine
Base Sequence
Cells
CaVβs
Gene expression
Human Umbilical Vein Endothelial Cells
Multi exon skipping
DMO
Delivery
LKB1
Multiresolution modeling
Invivo
Immunoglobulin Fc Fragments/pharmacology
DMD
Dystrophin central domain
Inhibitors
Genomic
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Hear
Cultured
Long QT
Dystrophie Musculaire de Duchenne DMD
Muscular dystrophy
Muscle
Molecular docking
Myogenesis
Humans
Inbred mdx
Cell Line
Mdx mouse
Liver
Cell homeostasis
Dystrophie Musculaire de Becker BMD
Muscles/physiopathology
Allele‐specific silencing therapy
Duchenne muscular dystrophy
MiARN
Gene Expression Regulation/drug effects
NAD+
CD38
Dynamin 2
Animals
Long noncoding RNA
Muscular Dystrophy
Exon skipping
Epigenetics
Clinical trials
Skeletal muscle
NNOS
Multi resolution modeling
Gene modifiers
Muscular Atrophy
Activin Receptors
CTNNB1
Calcium
LncARN
Drp1
Duchenne muscular dystrophy DMD
Mitochondrial fission
Calcium Channels
Hepatocellular carcinoma
Centronuclear myopathy
Animal/physiopathology
Metabolism
Ex-vivo
Cell Biology
Morphogenesis
MES
Muscle Biology
Dystrophie musculaire de Becker